Topic: Gene Therapy
WASHINGTON (Reuters) - A gene therapy treatment that stops the breakdown of muscle appeared safe in monkeys and may build up muscle, too, researchers reported on Wednesday.The approach is being developed in the hope of treating severe muscle weakness caused by multiple ...
LONDON (Reuters) - Scientists have managed to halt a rare and fatal brain disease with an experimental gene therapy technique using a deactivated version of the AIDS virus, a study published on Thursday showed.The international team used a disabled form of human ...
A breakthrough mix of stem cell and gene therapy halted a lethal brain-wasting illness in two young boys, and could prove effective against other genetic disorders, researchers reported Thursday.The boys, both seven when treatment began in France, are beset with X-linked adrenoleukodystrophy, ...
French scientists appear to halt rare brain disease in 2 boys with new gene therapy approachFrench scientists mixed gene therapy and bone marrow transplants in two boys to seemingly halt a brain disease that can kill by adolescence. They disabled the HIV ...
PHILADELPHIA (Reuters) - Nine-year-old Corey Haas can ride his bike alone now, thanks to an experimental gene therapy that has boosted his fading vision with a single treatment.The gene therapy helped improve worsening eyesight caused by a rare inherited disease called Leber ...
LONDON (Reuters) - Long-term tests on monkeys using Oxford BioMedica's gene therapy ProSavin suggest it can treat Parkinson's disease without causing the jerky, involuntary movements associated with current drugs, researchers said on Wednesday.Parkinson's is caused by lack of the brain chemical dopamine. ...
Gene therapy cures children with 'bubble boy' disease; hope for other blood disorders seenGene therapy seems to have cured eight of 10 children who had potentially fatal " The successful treatment is reported in Thursday's issue of the New England Journal of ...
Scientists have shown that gene therapy has potential for treating brain pathology triggered by the human immunodeficiency virus (HIV), which causes AIDS. NIMH-funded researchers Dr. D.S. Strayer and colleagues from Thomas Jefferson University loaded a harmless type of virus with genes engineered ...
Three young adults with an inherited form of blindness showed evidence of improved day and night vision following a specialized gene transfer procedure in a phase 1 clinical trial funded by the National Eye Institute (NEI), part of the National Institutes of ...
The study was scheduled to run for 54 weeks, which really was an arbitrary cut- off point, said Antonis Voutetakis, a scientist at the National Institute of Dental and Craniofacial Research (NIDCR) and lead author on the study. We chose to administer ...
